Patient | Gender | Data test | SMA1 type | Age (yrs) | ALSSS (/10) | RCPM (IQ) | RCPM (percentile) | TCGB (percentile) | CHOP INTEND (/64) |
---|---|---|---|---|---|---|---|---|---|
#1 | F | August 2012 | 1B | 5.0 | 2 | 130 | 100 | 75 | 6 |
#2 | F | June 2012 | 1B | 7.0 | 4 | 120 | 92 | 50 | 15 |
#3 | F | October 2012 | 1B | 6.1 | 3 | 110 | 73 | 25 | 11 |
#4 | F | January 2013 | 1B | 4.0 | 4 | 120 | 89 | 12 | |
#5 | F | February 2013 | 1B | 11.0 | 1 | 110 | 67 | 4 | |
#6 | M | March 2013 | 1B | 10.0 | 1 | 110 | 82 | 3 | |
#7 | M | September 2013 | 1A | 3.1 | 2 | 120 | 90 | 17 | |
#8 | F | May 2016 | 1B | 5.1 | 4 | 130 | 98 | 75 | 15 |
#9 | M | November 2016 | 1A | 4.0 | 1 | 110 | 67 | 15 | |
#10 | M | April 2017 | 1B | 5.0 | 2 | 120 | 93 | 75 | 14 |
#11 | F | May 2012 | 1C | 4.1 | 6 | 110 | 74 | 50 | 38 |
#12 | F | August 2012 | 1C | 6.1 | 6 | 120 | 89 | 25 | 18 |
#13 | F | October 2012 | 1C | 5.1 | 4 | 100 | 48 | 50 | 18 |
#14 | M | January 2013 | 1C | 4.1 | 6 | 120 | 93 | 14 | |
#15 | F | January 2013 | 1C | 7.1 | 7 | 130 | 96 | 49 | |
#16 | F | June 2013 | 1C | 9.1 | 7 | 100 | 61 | 25 | 51 |
#17 | F | February 2014 | 1C | 3.1 | 7 | 120 | 89 | 50 | |
#18 | F | June 2014 | 1C | 4.1 | 6 | 120 | 92 | 39 | |
#19 | F | May 2016 | 1C | 4.0 | 7 | 130 | 98 | 50 | 20 |
#20 | M | May 2016 | 1C | 5.0 | 7 | 100 | 56 | 50 | 27 |
#21 | M | March 2017 | 1C | 4.1 | 6 | 130 | 98 | 75 | 23 |
#22 | F | November 2017 | 1C | 3.1 | 7 | 120 | 84 | 37 | |
SMA1 subtypes A-B | Median | 5.0 | 2 | 120 | 75 | 13 | |||
25th perc | 4.3 | 1 | 110 | 50 | 7 | ||||
75th perc | 6.8 | 4 | 120 | 75 | 15 | ||||
SMA1 subtype C | Median | 4.1 | 7 | 120 | 50 | 32 | |||
25th perc | 4.1 | 6 | 108 | 38 | 20 | ||||
75th perc | 5.3 | 7 | 123 | 50 | 42 |